Workshop explores gene therapy for autism

On February 6–7, 2020, the Simons Foundation Autism Research Initiative (SFARI) convened a two-day workshop in New York City to explore the possibility of gene therapies for autism spectrum disorder (ASD). Inspired by the recent, stunning successes of gene therapy for the fatal neuromuscular disorder spinal muscular atrophy (SMA), and by the steady accumulation of genes confidently associated with ASD, SFARI welcomed a diverse collection of researchers to begin to think about whether a similar approach could be taken for severe neurodevelopmental disorders.

Read this report at SFARI.